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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Long noncoding RNA
DMD
Centronuclear myopathy
Molecular Sequence Data
Delivery
Cell Biology
Dystrophin central domain
DMO
Multi resolution modeling
CaVβs
Immunoglobulin Fc Fragments/pharmacology
Dystrophy
LKB1
Dystrophie Musculaire de Duchenne DMD
Inbred mdx
Animals
Becker muscular dystrophy
Homeostasis
Molecular docking
Becker BMD muscular dystrophy
Antisense oligonucleotides
Exon skipping
Inbred C57BL
Muscle
Gene expression
Male
Muscle Biology
Myogenesis
Animal/physiopathology
Dystrophie Musculaire de Becker BMD
Multi exon skipping
Muscular Dystrophy
Morphogenesis
Base Sequence
Cachexia
Activin Receptors
Cells
Duchenne DMD dystrophy
MES
Mice
Muscle development
Dystrophine
Cell homeostasis
Muscles/physiopathology
Humans
Muscular dystrophy
Diseases
Multiresolution modeling
Epigenetics
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Calcium Channels
Hepatocellular carcinoma
Duchenne muscular dystrophy DMD
Dystrophin-EGFP
Cultured
Hear
Allele‐specific silencing therapy
Human Umbilical Vein Endothelial Cells
Cardiomyopathy
LncARN
Mdx mouse
Genomic
Calcium
BMD
CTNNB1
L-Type
Gene modifiers
Energy Metabolism/drug effects
Autophagy
Clinical trials
Becker muscular dystrophy BMD
Cardiomyopathie
LncRNA
Muscular Atrophy
CD38
Muscle Strength
Inhibitors
Long QT
Génomique
DHPR α1S
Mitochondrial fission
NAD+
Myotendinous junction
Duchenne muscular dystrophy
Invivo
Skeletal muscle
Dystrophin
Metabolism
Drp1
MiARN
Liver
Gene Expression Regulation/drug effects
Cell Line
Dynamin 2
Knockout
Ex-vivo
Modificateurs de gènes
NNOS
Dystrophie musculaire de Becker
CaV subunits